Japan Hemophilia Gene Therapy Market Size and Forecasts Research Report 2021-2025

According to a new research report titled Hemophilia Gene Therapy Market Global Industry Perspective, Comprehensive Analysis And Forecast by 2021 – 2025

This has brought along several changes in This report also covers the impact of COVID-19 on the global market.

The latest report on the Hemophilia Gene Therapy Market 2021 industry takes a closer look at the value chain assessment for the forecast period, 2021 to 2025. Hemophilia is a rare bleeding disorder in which the blood does not clot normally. Hemophilia is a monogenic disease (a disease that is caused by a genetic defect in a single gene). There are two types of hemophilia caused by mutations in genes that encode protein factors which help the blood clot and stop bleeding when blood vessels are injured. Individuals with hemophilia experience bleeding episodes after injuries and spontaneous bleeding episodes that often lead to joint disease such as arthritis. The most frequent forms of hemophilia affect males.
About 80% of them have hemophilia A, which affects the clotting factor VIII. The second most common form, hemophilia B, is due to a deficiency of the clotting factor IX. Several biotechs are racing to launch the first gene therapy for hemophilia. Currently, uniQure in the Netherlands and Spark Therapeutics in the US have the most advanced programs. Spark scored a victory in December when it presented Phase I/II for its candidate SPK-9001. The gene therapy was able to reduce annual bleeding episodes by 97%, as compared to its competitor uniQure's candidate, AMT-060. However, uniQure has fought back. The company added a modification in its gene therapy that is known to increase clotting activity by 8- to 9- fold. This improved version has already been cleared to start a Phase III clinical trial in both Europe and the US.
Hemophilia B has traditionally been the main focus of biotechs, since most big pharma efforts were focused on the bigger hemophilia A market. In addition, applying gene therapy to hemophilia A is more challenging; The gene coding for the factor IX protein missing in hemophilia B is simply smaller than that for factor VIII missing in hemophilia A, and therefore easier to fit in the viral vectors used for gene delivery. US-based BioMarin is leading the development of a gene therapy. To overcome the size limit, the company has deleted a region from the factor VIII protein that is not necessary for clotting.
Hemophilia treatment is currently in the pre-clinical stage. And the multiple treatments that are underway might significantly improve the quality of life of patients with hemophilia, by getting rid of frequent infusions and hospital visits, and transitioning patients from severe to mild hemophilia.

Global Hemophilia Gene Therapy market size was xx million US$ and it is expected to reach xx million US$ by the end of 2025, with a CAGR of XX between 2021 and 2025.

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Key Competitors of the Global Hemophilia Gene Therapy Market are:
Spark Therapeutics, Ultragenyx, Shire PLC, Sangamo Therapeutics, Bioverativ, BioMarin, uniQure, Freeline Therapeutics

The ‘Global Hemophilia Gene Therapy Market Research Report’ is a comprehensive and informative study on the current state of the Global Hemophilia Gene Therapy Market industry with emphasis on the global industry. The report presents key statistics on the market status of the global Hemophilia Gene Therapy market manufacturers and is a valuable source of guidance and direction for companies and individuals interested in the industry.

Major Product Types covered are:

Hemophilia A
Hemophilia B

Major Applications of Hemophilia Gene Therapy covered are:

Hemophilia A Gene Therapy
Hemophilia B Gene Therapy

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Regional Hemophilia Gene Therapy Market (Regional Output, Demand & Forecast by Countries):-
North America (United States, Canada, Mexico)
South America ( Brazil, Argentina, Ecuador, Chile)
Asia Pacific (China, Japan, India, Korea)
Europe (Germany, UK, France, Italy)
Middle East Africa (Egypt, Turkey, Saudi Arabia, Iran) And More.

The research report studies the past, present, and future performance of the global market. The report further analyzes the present competitive scenario, prevalent business models, and the likely advancements in offerings by significant players in the coming years.

Key Questions answered by the Report

• What will be the growth rate of the Global Hemophilia Gene Therapy Market 2021 for the forecast period 2021 to 2025?
• What will be the market size during this estimated period?
• What will be the growth areas within the market space and where should the participant focus to gain maximum ROI?
• Who are the prominent industries players dominating the Global Hemophilia Gene Therapy Market and what are their business strategies to stay ahead in the competition against their rivals?
• What are kind of challenges hindering the development of the industry worldwide?
• Competitive landscape of the Global Hemophilia Gene Therapy Market
• What are the opportunities business owners can rely upon to earn more profits and stay competitive during the estimated period?
• Potential and niche segments/regions exhibiting promising growth
• A neutral perspective towards Global Hemophilia Gene Therapy market performance

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